We are the only 501(c)3 organization solely dedicated to finding treatments for Nemaline Myopathy, while also providing support and resources to the NM community.
A Foundation Building Strength’s mission is to find treatments for Nemaline Myopathy (NM).
AFBS works to address issues for our NM families from all angles, including advancing research, providing information about care, offering family support groups and ways to connect, and creating opportunities for in-person interaction and education at conferences.
Working towards this mission, we fund research aimed at understanding protein function and disease progressions, prerequisites to regulatory approval such as natural history, gene expression and editing such as CRISPR and Cas9, exon skipping, gene therapy and related approaches.
We are highly driven to efficiently and effectively move research progress forward and have done this through funding only the most promising studies, bringing together top scientists around the world to collaborate and making connections with other rare disease researchers, pharmaceutical and biotech companies.